New data from Biogen reveals higher Spinraza doses may enhance motor function in SMA patients. Read more here.

Learn what you need to do to have a fun, safe, and stress-free day at an amusement park when you have spinal muscular atrophy.

After all the anticipation, Novartis has the FDA approval it has been seeking for Zolgensma, its gene therapy for spinal muscular atrophy, and has priced it at the low end of expectations. The FDA ...

Treatment with salanersen slowed neurodegeneration and improved motor function in children with SMA in a Phase 1 trial, ...