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It will grow to $9.02 billion in 2029 at a compound annual growth rate (CAGR) of 15.3%.” — The Business Research Company LONDON, GREATER LONDON, UNITED KINGDOM, July 3, 2025 /EINPresswire.com/ -- Save ...
Objective The aim of this study was to assess early language acquisitions in treated individuals with spinal muscular atrophy (SMA) type 1 and in infants identified by newborn screening (NBS). Methods ...
Treatment with salanersen slowed neurodegeneration and improved motor function in children with SMA in a Phase 1 trial, ...
New analyses from DEVOTE Part C further characterize the improvements in motor function in participants with SMA who transitioned to the investigational higher dose regimen of nusinersen from 12 mg SP ...
New analyses from DEVOTE Part C further characterize the improvements in motor function in participants with SMA who ...
Biogen has pointed to an early readout from a small phase 1 trial as evidence that its antisense oligonucleotide salanersen ...
The cumulative data from the Phase 1 study indicate that salanersen has a generally well tolerated safety profile at both the 40 mg and 80 mg doses, with most adverse events (AEs) mild to moderate in ...
Article Published: June 2000 Motor coordination without action potentials in the mammalian spinal cord Matthew C. Tresch & Ole Kiehn Nature Neuroscience 3, 593–599 (2000) Cite this article ...
In perhaps a first in the country, a newborn found carrying the SMN1 gene mutation for Spinal Muscular Atrophy (SMA) through prenatal genetic screening is being administered presymptomatic ...
Session ID: 2025-07-05:9a280840deb0acb14c589c11 Player Element ID: vjs_video_3 ...
Spinal Muscular Atrophy treatment is evolving fast, with gene therapy, oral drugs, and next-gen muscle enhancers offering new hope and long-term outcomes. With each breakthrough in SMA treatment, we ...
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