Danicopan is being developed to enhance complement C5 inhibitor therapy, like eculizumab and ravulizumab, by selectively inhibiting factor D within the complement system. Among patients with ...
The study provides the strongest evidence to date supporting the potential of proximal pathway inhibitors to enhance clinical outcomes and quality of life for patients with PNH. Proximal pathway ...
Artificial intelligence may help physicians better predict infant diseases and introduce necessary interventions in a timely manner. Artificial intelligence (AI) is a powerful tool that can be ...
Blood tests revealed the presence of autoantibodies consistent with all 3 conditions. Researchers from China reported the case of a patient with primary biliary cholangitis (PBC), neuromyelitis optica ...
Factor-H works to alleviate extreme poverty among people with Huntington disease in Venezuela, Colombia, and Peru. Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Ignacio Muñoz ...
The evidence presented in the review solves a number of issues that have remained unclear until now. A new review article published in the journal Exploration of Immunology hypothesized that bile ...
Of course, I had never heard of chronic inflammatory demyelinating polyneuropathy (CIDP), so I immediately went home and looked it up.
The PAH group received significantly less fluids within the first 24 hours compared with controls. On the other hand, they were more likely to require vasopressors. A recent study highlights the ...
The Supplemental Oxygen Access Reform (SOAR) Act is stalled in the US Congress. Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Amy Case, MD, chief medical officer of the ...
Patients with Huntington disease in Venezuela’s impoverished Lake Maracaibo region (Photo by Vladimir Marcano) Venezuela is home to one of the world’s highest concentrations of people with Huntington ...
The study notes the ongoing need for standardized management guidelines and further research into alternative therapies for IgG4-RD, especially in recurrent cases. In Surgery Case Reports, researchers ...
Ordering patterns for KIT and TPSAB1 gene testing revealed strategic approaches to patient care for mast cell disorders. Allergists play a crucial role in the diagnosis of mast cell disorders such as ...