The research looked specifically at blood stem cells, which live in the bone marrow and make different types of blood cells.

Microglia replacement therapy helps treat people with a rare genetic condition called ALSP, suggesting the approach could ...

Logan Cyr, 16, joined a global accelerator program for teens that enables him to research cures for genetic malformations.

The gene therapy regimen seems to be working wonders, including restoring nearly all hearing to a seven-year-old patient ...

A new study by researchers at the Icahn School of Medicine at Mount Sinai, Memorial Sloan Kettering Cancer Center, and ...

Clementine Blackham, a 2-year-old from McCandless, is loving life. She loves her big sister, FinnLee, water balloons and ...

Our genes underlie all aspects of life, from our looks to how our cells behave. This includes diseases, as genetic changes ...

The discovery may explain why cutting edge CAR T-cell therapy has managed to revolutionized treatment for blood cancer but ...

Fourteen million people worldwide suffer from enlarged hearts, or hypertrophic cardiomyopathy (HCM), a genetic disease that ...