The discovery may explain why cutting edge CAR T-cell therapy has managed to revolutionized treatment for blood cancer but ...

For decades, the dream of fixing harmful mutations in mitochondrial DNA felt out of reach. Scientists have long known these ...

A new study suggests a gene mutation could have a protective effect against Alzheimer's. The research looked specifically at ...

Logan Cyr, 16, joined a global accelerator program for teens that enables him to research cures for genetic malformations.

Microglia replacement therapy helps treat people with a rare genetic condition called ALSP, suggesting the approach could ...

The gene therapy regimen seems to be working wonders, including restoring nearly all hearing to a seven-year-old patient ...

Clementine Blackham, a 2-year-old from McCandless, is loving life. She loves her big sister, FinnLee, water balloons and ...

Our genes underlie all aspects of life, from our looks to how our cells behave. This includes diseases, as genetic changes ...

Rare genetic diseases are challenging for patients and their families—made all the more overwhelming because symptoms tend to ...

In a paper published last month, researchers at UT Southwestern Medical Center introduced lipid nanoparticles — hollow, fatty ...

New research from UC Davis Comprehensive Cancer Center has uncovered an evolutionary change that may explain why certain ...

Picture juicy red tomatoes on the vine. What do you see? Some tomato varieties have straight vines. Others are branched. The ...