In vivo base editing enables precise, single-nucleotide changes to DNA without double-strand breaks. A recent application in ...

Fourteen million people worldwide suffer from enlarged hearts, or hypertrophic cardiomyopathy (HCM), a genetic disease that ...

The discovery may explain why cutting edge CAR T-cell therapy has managed to revolutionized treatment for blood cancer but ...

Scientists with the NIH-backed SMaHT Network are mapping every DNA mutation in the human body, creating a groundbreaking ...

Researchers working on an incurable blood cancer can now use a new lab model that could make testing potential new treatments ...