Germline gene therapy and somatic gene therapy are two quite different proposals, and the legitimate concerns and risks of the former should not be used to stall progress on the latter.

What is the Committee’s biggest concern about genome editing? This development seems to require particular precautions and raises serious concerns, especially if the editing of the human genome should ...

Mismatch repair germline alterations occur frequently in uveal melanoma, suggesting it could be part of the Lynch syndrome spectrum.

The utility of a pure population of highly regenerative satellite stem cells (SSCs) is a prerequisite for successful cell-based muscle therapies. P ...

AbstractPurpose:. In a multicenter prospective cohort study, we assessed the diagnostic yield of the Nordic guidelines for germline investigation in myeloid neoplasms and mapped the spectrum of ...