Molecular markers in cerebrospinal fluid may help predict if people with SMA type 2 or type 3 will respond to treatment with ...

A group of questionnaires called PROfuture can meaningfully measure a variety of symptoms of SMA that impact patients, a study reported.

As treatment for spinal muscular atrophy (SMA) has drastically improved over the last decade, so too have survival rates and the number of people with SMA living well into adulthood. | A new education ...

Biogen's early-stage spinal muscular atrophy drug salanersen showed safety, motor improvements and 70% reduction in neurodegeneration markers after one-year dosing.

Spinal muscular atrophy (SMA) is an autosomal recessive genetic disease that causes progressive degeneration of motor neurons, affecting approximately 1 in 10,000 births.

The FDA has accepted for Priority Review the BLA for apitegromab for the improvement of motor function in patients with spinal muscular atrophy.

The FDA has approved Evrysdi in tablet form for patients with spinal muscular atrophy aged 2 years and older who weigh more than 44 pounds, according to the manufacturer.Evrysdi (risdiplam ...

Spinal Muscular Atrophy (SMA) is a common genetic disorder affecting both children and adults, frequently encountered by pediatricians, neurologists, physiotherapists, and the general public.

Muscle weakness could be a sign of spinal muscular atrophy, which can strike all ages but is the No. 1 genetic cause of death in infants. Here's what it is and what you can do about it.

Spinal muscular atrophy (SMA) is a severe neurological disease caused by reduced survival of motor neuron (SMN) protein levels. There is presently no cure for the condition, although current ...

An international study has discovered that people living with the neurodegenerative condition Spinal Muscular Atrophy (SMA) are at higher risk of developing fatty liver disease, suggesting that ...

In managing patients with a serious condition like spinal muscular atrophy, it’s often the caregiver who suffers along with the patient. A new study sought to better quantify this relationship.