Learn what you need to do to have a fun, safe, and stress-free day at an amusement park when you have spinal muscular atrophy.

Objective The aim of this study was to assess early language acquisitions in treated individuals with spinal muscular atrophy (SMA) type 1 and in infants identified by newborn screening (NBS). Methods ...

Treatment with salanersen slowed neurodegeneration and improved motor function in children with SMA in a Phase 1 trial, ...

Panelists discuss how intrathecal delivery of onasemnogene abeparvovec in the STEER study demonstrates statistically ...

Biogen said that new data examining of its already approved spinal muscular atrophy treatment Spinraza (nusinersen) indicates ...

In perhaps a first in the country, a newborn found carrying the SMN1 gene mutation for Spinal Muscular Atrophy (SMA) through prenatal genetic screening is being administered presymptomatic ...

The baby from Ranaghat in Nadia is suffering from spinal muscular atrophy (SMA) Type I, a condition that causes progressive weakening of the muscles and nerves A 16-month-old girl with a rare genetic ...

Panelists discuss how combination therapies targeting different aspects of spinal muscular atrophy (SMA), such as myostatin inhibitors (targeting muscle) alongside SMN protein-enhancing treatments ...

Dilsher S. Dhoot, MD, FASRS, provided an update on the current treatment landscape for geographic atrophy (GA) in a recent interview with the Eye Care Network. “Geographic atrophy causes progressive ...

5q-Spinal muscular atrophy (SMA) is a progressive, autosomal recessive neuromuscular disease with an incidence of 1 in 14,848 births.1 SMA is characterised by proximal muscle weakness and in severe ...

Credit: Bioengineering (2025). DOI: 10.3390/bioengineering12040410 There are over 15 million people living with spinal cord injury (SCI) worldwide.