New data from Biogen reveals higher Spinraza doses may enhance motor function in SMA patients. Read more here.

Spinal muscular atrophy (SMA) is a severe motor neuron disease caused by mutations in the SMN1 gene, leading to reduced SMN protein levels. Although postnatal treatments like the antisense ...

Roche announced that the European Commission (EC) has approved a label extension for Evrysdi (risdiplam) to include a new, room-temperature stable tablet for people living with spinal muscular atrophy ...

SMA is caused by a mutation of the survival motor neuron 1 (SMN1) gene, which leads to a deficiency of SMN protein. This protein is found throughout the body and is essential to the function of nerves ...

Research shows that kids with spinal muscular atrophy do best with a team approach to their care. Parents, doctors, nurses, therapists, counselors, and a dietitian are all important members of the ...

Panelists discuss how spinal muscular atrophy is an autosomal recessive genetic disease affecting motor neurons with 3 ...

Thiruvananthapuram: For the first time in India, pre-symptomatic treatment to an infant, diagnosed with spinal muscular atrophy (SMA) within days of b.

Roche’s Evrysdi (risdiplam) tablets have been approved by the European Commission (EC) to treat spinal muscular atrophy (SMA). The new, room-temperature stable formulation of Evrysdi may offer ...

Motor neuron disease usually refers to amyotrophic lateral sclerosis, but it can also refer to other kind of neurodegenerative disease that affect the motor neurons, such as progressive primary ...

EP: 3. Key Takeaways From DMD Treatment Data EP: 4. Overview of Spinal Muscular Atrophy EP: 5. Gaps in Care for Childhood SMA EP: 6. The Impact of Intrathecal Onasemnogene Abeparvovec Therapy in SMA ...